Development and validation of a novel AAV gene therapy for mucopolysaccharidosis type IIIB in large animal

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Bibliographic Details
Published inMolecular genetics and metabolism Vol. 141; no. 2; p. 107768
Main Authors Banchi, Elena Gaia, Alonso, Rafael, Jacquot, Sylvie, Fransquin, Kevin, Courtot, Enora, de Saint Denis, Timothee, Ausseil, Jérôme, Piguet, Françoise
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2024
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ISSN1096-7192
1096-7206
DOI10.1016/j.ymgme.2023.107768

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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2023.107768