Generation of a homozygous CRISPR/Cas9-mediated knockout human iPSC line for the STUB1 locus
STUB1/CHIP is a central component of cellular protein homeostasis and interacts with key proteins involved in the pathogenesis of many neurodegenerative diseases. Missense and truncating mutations in STUB1 lead to SCAR16. For ideal in vitro disease modelling with isogenic controls, we generated a CH...
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Published in | Stem cell research Vol. 34; p. 101378 |
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Main Authors | , , , |
Format | Journal Article |
Language | English |
Published |
England
Elsevier B.V
01.01.2019
Elsevier |
Online Access | Get full text |
ISSN | 1873-5061 1876-7753 1876-7753 |
DOI | 10.1016/j.scr.2018.101378 |
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Summary: | STUB1/CHIP is a central component of cellular protein homeostasis and interacts with key proteins involved in the pathogenesis of many neurodegenerative diseases. Missense and truncating mutations in STUB1 lead to SCAR16. For ideal in vitro disease modelling with isogenic controls, we generated a CHIP knockout cell line from a healthy control with no CHIP functionality, but remaining genomic integrity and verified pluripotency. |
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Bibliography: | ObjectType-Article-1 SourceType-Scholarly Journals-1 ObjectType-Feature-2 content type line 23 |
ISSN: | 1873-5061 1876-7753 1876-7753 |
DOI: | 10.1016/j.scr.2018.101378 |