Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study
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| Published in | Molecular genetics and metabolism Vol. 123; no. 2; p. S48 |
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| Main Authors | , , , , , , , , , , , , , |
| Format | Journal Article |
| Language | English |
| Published |
Elsevier Inc
01.02.2018
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| Online Access | Get full text |
| ISSN | 1096-7192 1096-7206 |
| DOI | 10.1016/j.ymgme.2017.12.109 |
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| Author | Chabrol, Brigitte Eyer, Didier Cances, Claude Freihuber, Cecile Broue, Pierre Vanier, Marie Therese Latour, Philippe Labarthe, Fancois Sevin, Caroline Pichard, Samia Brassier, Anais Levade, Thierry Heron, Benedicte Dahmani, Bahia |
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| Title | Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study |
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