Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study

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Bibliographic Details
Published inMolecular genetics and metabolism Vol. 123; no. 2; p. S48
Main Authors Freihuber, Cecile, Dahmani, Bahia, Brassier, Anais, Broue, Pierre, Cances, Claude, Chabrol, Brigitte, Eyer, Didier, Labarthe, Fancois, Latour, Philippe, Levade, Thierry, Pichard, Samia, Sevin, Caroline, Vanier, Marie Therese, Heron, Benedicte
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2018
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ISSN1096-7192
1096-7206
DOI10.1016/j.ymgme.2017.12.109

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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2017.12.109