Safety and efficacy of gene-based therapeutics for inherited disorders

• Other Authors: Brunetti-Pierri, Nicola (Editor)
• Format: Electronic eBook
• Language: English
• Published: Cham, Switzerland : Springer, [2017]
• Subjects: Genetic disorders > Gene therapy.; Genetic transformation.; elektronické knihy; electronic books
• ISBN: 9783319534572; 9783319534558
• Physical Description: 1 online resource

In this book, leading international experts analyze state-of-the-art advances in gene transfer vectors for applications in inherited disorders and also examine the toxicity profiles of these methods. The authors discuss the strengths and weaknesses of available vectors in the clinical setting, and s...