Trappsol®Cyclo™ and NPC: Efficacy shown across individual 5D domains and utilization of future assessment tools to demonstrate clinically relevant outcomes

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Published inMolecular genetics and metabolism Vol. 144; no. 2; p. 108757
Main Authors Hastings, Caroline A., Ezgu, Fatih S., Giugliani, Roberto, Kiec-Wilk, Beata, Pawlinski, Lukasz, Mengel, Eugen, Mohand, Patricia Pérez, Ucar, Seema, Sharma, Reena, Smith, Nicholas J.C., Chien, Yin-Hsiu, Walterfang, Mark, Alsayed, Moeen, Goker-Alpan, Ozlem, Mendonca, Leonardo O., Raiman, Julian A., Spiegel, Ronen, Barone, Rita Maria Elisa, Burlina, Alberto, Calandra, Cristian R., Bayarri, Jordi Gascon, Peters, Heidi, Murray, Bryan J., Brecht, Andreas F., Mejia, Joseph
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2025
Online AccessGet full text
ISSN1096-7192
DOI10.1016/j.ymgme.2024.108757

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ArticleNumber 108757
Author Peters, Heidi
Pawlinski, Lukasz
Mengel, Eugen
Barone, Rita Maria Elisa
Alsayed, Moeen
Walterfang, Mark
Brecht, Andreas F.
Burlina, Alberto
Bayarri, Jordi Gascon
Sharma, Reena
Kiec-Wilk, Beata
Ezgu, Fatih S.
Mendonca, Leonardo O.
Ucar, Seema
Hastings, Caroline A.
Giugliani, Roberto
Chien, Yin-Hsiu
Spiegel, Ronen
Murray, Bryan J.
Calandra, Cristian R.
Smith, Nicholas J.C.
Goker-Alpan, Ozlem
Mohand, Patricia Pérez
Raiman, Julian A.
Mejia, Joseph
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  organization: Cyclo Therapeutics, Gainesville, FL, USA
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StartPage 108757
Title Trappsol®Cyclo™ and NPC: Efficacy shown across individual 5D domains and utilization of future assessment tools to demonstrate clinically relevant outcomes
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