Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes - Canepari, Cesare; Milani, Michela; Simoni, Chiara; Starinieri, Francesco; Volpin, Monica; Fabiano, Anna; Biffi, Mauro; Russo, Fabio; Norata, Rossana; Rocchi, Martina; Brombin, Chiara; Cugnata, Federica; et al. (Nature communications, 2025)
Keywords: 38/35; 38/77; 38/89; 42; 42/44; 59; 631/61/201; 631/61/2300/1514; 64/110; 64/60; 692/4017; 82/51; Animal models; Animals; Coagulation; Disease Models, Animal; Expression vectors; Gene therapy; Gene transfer; Genetic Therapy - methods; Genetic Vectors - genetics; Hemophilia; Hemophilia A - genetics; Hemophilia A - therapy; Hepatocytes; Hepatocytes - metabolism; Humanities and Social Sciences; Humans; Lentivirus - genetics; Liver; Liver - metabolism; Male; Mice; Mice, Inbred C57BL; multidisciplinary; Phagocytosis; Science; Science (multidisciplinary); Transduction; Transduction, Genetic - methods; Transgenes