Adeno‐associated virus serotype 1‐based gene therapy for FTD caused by GRN mutations - Hinderer, Christian; Miller, Rod; Dyer, Cecilia; Johansson, Julia; Bell, Peter; Buza, Elizabeth; Wilson, James M. (Annals of clinical and translational neurology, 2020)
Keywords: Age; Brain; Dementia; Enzymes; Gene therapy; Histology; Mutation; Pathology; Pathophysiology; Proteins; United States--US; Pennsylvania