Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs - Majowicz, Anna; Nijmeijer, Bart; Lampen, Margit H.; Spronck, Lisa; de Haan, Martin; Petry, Harald; van Deventer, Sander J.; Meyer, Christian; Tangelder, Marco; Ferreira, Valerie (Molecular therapy. Methods & clinical development, 2019)
Keywords: AAV; anti-AAV NABs; Bioassays; Clinical trials; Coagulation factors; Factor IX deficiency; FIX; Gene therapy; Hemophilia; hFIX; Immunoglobulins; Laboratories; NABs; Patients; Studies; Vectors (Biology); NABs; hemophilia; FIX; anti-AAV NABs; AAV; gene therapy; hFIX