Outcomes of transplantation using various hematopoietic cell sources in children with Hurler syndrome after myeloablative conditioning - Boelens, Jaap Jan; Aldenhoven, Mieke; Purtill, Duncan; Ruggeri, Annalisa; DeFor, Todd; Wynn, Robert; Wraith, Ed; Cavazzana-Calvo, Marina; Rovelli, Attilio; Fischer, Alain; Tolar, Jakub; Prasad, Vinod K.; et al. (Blood, 2013)
Keywords: Adolescent; Child; Child, Preschool; Female; Hematopoietic Stem Cell Transplantation - adverse effects; Hematopoietic Stem Cell Transplantation - methods; Hematopoietic Stem Cells - cytology; Histocompatibility Testing; Humans; Infant; Male; Mucopolysaccharidosis I - epidemiology; Mucopolysaccharidosis I - mortality; Mucopolysaccharidosis I - therapy; Myeloablative Agonists - adverse effects; Myeloablative Agonists - therapeutic use; Retrospective Studies; Tissue and Organ Procurement - methods; Tissue Donors; Transplantation; Transplantation Conditioning - adverse effects; Transplantation Conditioning - methods; Treatment Outcome; Young Adult