Acute and chronic tirasemtiv treatment improves in vivo and in vitro muscle performance in actin-based nemaline myopathy mice - de Winter, Josine M; Gineste, Charlotte; Minardi, Elisa; Brocca, Lorenza; Rossi, Maira; Borsboom, Tamara; Beggs, Alan H; Bernard, Monique; Bendahan, David; Hwee, Darren T; Malik, Fady I; Pellegrino, Maria Antonietta; et al. (Human molecular genetics, 2021)
Keywords: Actins - genetics; Animals; Bioengineering; Humans; Imaging; Imidazoles; Life Sciences; Mice; Muscle, Skeletal - pathology; Mutation; Myopathies, Nemaline - drug therapy; Myopathies, Nemaline - genetics; Pyrazines - therapeutic use