Risdiplam in non‐sitter patients aged 16 years and older with 5q spinal muscular atrophy - Ñungo Garzón, Nancy Carolina; Pitarch Castellano, Inmaculada; Sevilla, Teresa; Vázquez‐Costa, Juan Francisco (Muscle & nerve, 2023)
Keywords: Adolescent; Adult; Azo Compounds; Humans; Middle Aged; Muscular Atrophy, Spinal - drug therapy; non‐sitter; Pyrimidines; risdiplam; Spinal Muscular Atrophies of Childhood - drug therapy; spinal muscular atrophy; type 2; Upper Extremity; Young Adult; adolescent; spinal muscular atrophy; type 2; risdiplam; adult; non-sitter