177. Lentiviral Vector Mediated ADA Gene Transfer in ADA-Deficient SCID Mice - Carbonaro, Denise A; Jin, Xiangyang; Senadherra, Dinithi; Pepper, Karen; Petersen, Denise; Yu, Xiao-jin; Skelton, Dianne; Kohn, Donald B (Molecular therapy, 2004)
Keywords: Bone marrow; DNA repair; Enzymes; Gene therapy; Genetic testing; Hemoglobin; Hospitals; Mutation; Sickle cell anemia; Sickle cell disease