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Transthyretin stabilization activity of the catechol-O-methyltransferase inhibitor tolcapone (SOM0226) in hereditary ATTR amyloidosis patients and asymptomatic carriers: proof-of-concept study
Gamez, Josep, Salvadó, María, Reig, Núria, Suñé, Pilar, Casasnovas, Carles, Rojas-Garcia, Ricard, Insa, Raúl
Published in Amyloid (03.04.2019)
Published in Amyloid (03.04.2019)
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Journal Article
CSF/plasma levels, transthyretin stabilisation and safety of multiple doses of tolcapone in subjects with hereditary ATTR amyloidosis
Takahashi, Yusuke, Ohashi, Nobuhiko, Takasone, Ken, Yoshinaga, Tsuneaki, Yazaki, Masahide, Roberts, Michael, Glidden, Paul F., Sekijima, Yoshiki
Published in Amyloid (03.07.2022)
Published in Amyloid (03.07.2022)
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Journal Article
Noninvasive detection of cardiac involvement in patients with hereditary transthyretin associated amyloidosis using cardiac magnetic resonance imaging: a prospective study
Deux, Jean-François, Damy, Thibaud, Rahmouni, Alain, Mayer, Julie, Planté-Bordeneuve, Violaine
Published in Amyloid (01.12.2014)
Published in Amyloid (01.12.2014)
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Journal Article
Sudoscan in the evaluation and follow-up of patients and carriers with TTR mutations: experience from an Italian Centre
Luigetti, Marco, Bisogni, Giulia, Romano, Angela, Di Paolantonio, Andrea, Barbato, Francesco, Primicerio, Giulia, Rossini, Paolo Maria, Servidei, Serenella, Sabatelli, Mario
Published in Amyloid (02.10.2018)
Published in Amyloid (02.10.2018)
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Journal Article
Binding of a Pyrene-Based Fluorescent Amyloid Ligand to Transthyretin: A Combined Crystallographic and Molecular Dynamics Study
Nghia Nguyen Thi Minh, Afshan Begum, Jun Zhang, Petter Leira, Yogesh Todarwal, Mathieu Linares, Patrick Norman, Dean Derbyshire, Eleonore von Castelmur, Mikael Lindgren, Per Hammarström, Carolin König
Published in The Journal of Physical Chemistry B (21.07.2023)
Published in The Journal of Physical Chemistry B (21.07.2023)
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Journal Article
New objective simple evaluation methods of amyloid PET/CT using whole-brain histogram and Top20%-Map
Chio Okuyama, Tatsuya Higashi, Koichi Ishizu, Naoya Oishi, Kuninori Kusano, Miki Ito, Shinya Kagawa, Tomoko Okina, Norio Suzuki, Hiroshi Hasegawa, Yasuhiro Nagahama, Hiroyuki Watanabe, Masahiro Ono, Hiroshi Yamauchi
Published in Annals of Nuclear Medicine (08.05.2024)
Published in Annals of Nuclear Medicine (08.05.2024)
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Journal Article