Search Results - "factor IX deficiency" :: K.UTB vyhledávací portál | TBU Library Retrieval Portal

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Long‐term safety and sustained efficacy for up to 5 years of treatment with recombinant factor IX Fc fusion protein in subjects with haemophilia B: Results from the B‐YOND extension study

by Pasi, K. John, Fischer, Kathelijn, Ragni, Margaret, Kulkarni, Roshni, Ozelo, Margareth C., Mahlangu, Johnny, Shapiro, Amy, P’Ng, Stephanie, Chambost, Hervé, Nolan, Beatrice, Bennett, Carolyn, Matsushita, Tadashi, Winding, Bent, Fruebis, Joachim, Yuan, Huixing, Rudin, Dan, Oldenburg, Johannes
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2020)

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Results of genetic analysis of 11341 participants enrolled in the My Life, Our Future hemophilia genotyping initiative in the United States

by Johnsen, Jill M, Fletcher, Shelley N, Dove, Angela, McCracken, Haley, Martin, Beth K, Kircher, Martin, Josephson, Neil C, Shendure, Jay, Ruuska, Sarah E, Valentino, Leonard A, Pierce, Glenn F, Watson, Crystal, Cheng, Dunlei, Recht, Michael, Konkle, Barbara A
Published in Journal of thrombosis and haemostasis (01.09.2022)

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Clot waveform of APTT has abnormal patterns in subjects with COVID-19

by Shimura, Takuya, Kurano, Makoto, Kanno, Yoshiaki, Ikeda, Mahoko, Okamoto, Koh, Jubishi, Daisuke, Harada, Sohei, Okugawa, Shu, Moriya, Kyoji, Yatomi, Yutaka
Published in Scientific reports (04.03.2021)

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Factor IX assay discrepancies in the setting of liver gene therapy using a hyperfunctional variant factor IX‐Padua

by Robinson, Mary M., George, Lindsey A., Carr, Marcus E., Samelson‐Jones, Benjamin J., Arruda, Valder R., Murphy, John E., Rybin, Denis, Rupon, Jeremy, High, Katherine A., Tiefenbacher, Stefan
Published in Journal of thrombosis and haemostasis (01.05.2021)

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Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs

by Majowicz, Anna, Nijmeijer, Bart, Lampen, Margit H., Spronck, Lisa, de Haan, Martin, Petry, Harald, van Deventer, Sander J., Meyer, Christian, Tangelder, Marco, Ferreira, Valerie
Published in Molecular therapy. Methods & clinical development (13.09.2019)

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Prophylaxis in factor IX deficiency product and patient variation

by Kisker, C.T., Eisberg, A., Schwartz, B.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2003)

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Pattern of use and clinical outcomes with rIX‐FP in pediatric/adolescent patients with haemophilia B in Italy: Results from IDEAL real‐world study

by Giordano, Paola, Pollio, Berardino, Sottilotta, Gianluca, Biasoli, Chiara, Daniele, Filomena, De Cristofaro, Raimondo, Peyvandi, Flora, Villa, Maria Rosaria, Castaman, Giancarlo
Published in European journal of haematology (01.05.2024)

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Identifying hemophilia B carriers: Utility of aPTT, factor IX levels and ratios of factor IX to other Vitamin K dependent factors

by Shu, Michael, Malcolmson, Caroline, Bosch, Alessandra, Markovic, Teodora, Wakefield, Cindy, Bouskill, Vanessa, Carcao, Manuel
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2024)

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Clinical use of recombinant factor VIII Fc and recombinant factor IX Fc in patients with haemophilia A and B

by Wang, C., Young, G.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2018)

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Safety, pharmacokinetics, and pharmacodynamics of a next‐generation subcutaneously administered coagulation factor IX variant, dalcinonacog alfa, in previously treated hemophilia B patients

by You, Chur Woo, Hong, Seung‐Beom, Kim, Suyeong, Shin, Ho‐Jin, Kim, Jin Seok, Han, Jung Woo, Kim, Soo‐Jeong, Kim, Do Young, Lee, Martin, Levy, Howard
Published in Journal of thrombosis and haemostasis (01.04.2021)

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The B‐Natural study—The outcome of immune tolerance induction therapy in patients with severe haemophilia B

by Astermark, Jan, Holstein, Katharina, Abajas, Yasmina L., Kearney, Susan, Croteau, Stacy E., Liesner, Riana, Funding, Eva, Kempton, Christine L., Acharya, Suchitra, Lethagen, Stefan, LeBeau, Petra, Bowen, Joel, Berntorp, Erik, Shapiro, Amy D.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2021)

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IDEAL study: A real‐world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX‐FP) in patients with haemophilia B in Italy

by Tagliaferri, Annarita, Molinari, Angelo Claudio, Peyvandi, Flora, Coppola, Antonio, Demartis, Francesco, Biasoli, Chiara, Borchiellini, Alessandra, Cultrera, Dorina, De Cristofaro, Raimondo, Daniele, Filomena, Giordano, Paola, Marchesini, Emanuela, Margaglione, Maurizio, Marino, Renato, Pollio, Berardino, Radossi, Paolo, Santoro, Cristina, Santoro, Rita Carlotta, Siragusa, Sergio, Sottilotta, Gianluca, Tosetto, Alberto, Piscitelli, Lydia, Villa, Maria Rosaria, Zanon, Ezio, Finardi, Adele, Schiavetti, Irene, Vaccari, Daniella, Castaman, Giancarlo
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2023)

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Prophylaxis with recombinant factor IX Fc fusion protein reduces the risk of bleeding and delays time to first spontaneous bleed event in previously untreated patients with haemophilia B: A post hoc analysis of the PUPs B‐LONG study

by Nolan, Beatrice, Recht, Michael, Rendo, Pablo, Falk, Aletta, Foster, Meredith, Casiano, Sandra, Rauch, Antoine, Shapiro, Amy
Published in European journal of haematology (01.10.2024)

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Health‐related quality of life in paediatric haemophilia B patients treated with rIX‐FP

by von Mackensen, Sylvia, Shah, Jinesh, Seifert, Wilfried, Kenet, Gili
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2019)

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Protein-Engineered Coagulation Factors for Hemophilia Gene Therapy

by Samelson-Jones, Benjamin J., Arruda, Valder R.
Published in Molecular therapy. Methods & clinical development (15.03.2019)

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Pharmacokinetics, safety and efficacy of a recombinant factor IX product, trenonacog alfa in previously treated haemophilia B patients

by Collins, P. W., Quon, D. V. K., Makris, M., Chowdary, P., Kempton, C. L., Apte, S. J., Ramanan, M. V., Hay, C. R. M., Drobic, B., Hua, Y., Babinchak, T. J., Gomperts, E. D.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2018)

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The Risk of Venipuncture in Newborn with Severe Hemophilia: Case Report of a Large Elbow Hemorrhage and Literature Review of Compartment Syndrome

by Lassandro, Giuseppe, Amoruso, Anna, Palladino, Valentina, Palmieri, Viviana Valeria, Giordano, Paola
Published in Hematology reports (09.06.2021)

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In silico evaluation of limited blood sampling strategies for individualized recombinant factor IX prophylaxis in hemophilia B patients

by Preijers, T., Hazendonk, H. C. A. M., Fijnvandraat, K., Leebeek, F. W. G., Cnossen, M. H., Mathôt, R. A. A.
Published in Journal of thrombosis and haemostasis (01.09.2017)

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AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects

by Hasbrouck, N C, High, K A
Published in Gene therapy (01.06.2008)

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Activation of Factor VII During Alimentary Lipemia Occurs in Healthy Adults and Patients With Congenital Factor XII or Factor XI Deficiency, But Not in Patients With Factor IX Deficiency

by Miller, George J., Martin, Janet C., Mitropoulos, Kostas A., Esnouf, M.Peter, Cooper, Jacqueline A., Morrissey, James H., Howarth, David J., Tuddenham, Edward G.D.
Published in Blood (15.05.1996)

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