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RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEPTIDES
LI Heping, REN Qiongqiong, WU Bing, SHU Yanqun, HOU Jinzhao, XIAO Lumei, LI Peilu
Year of Publication 06.12.2024
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Year of Publication 06.12.2024
Patent
ADENO-ASSOCIATED VIRUS FORMULATIONS
Meinhard HASSLACHER, Christian FIEDLER, Eva FRITSCHER, Dominik MITTERGRADNEGGER, Tanvir TABISH
Year of Publication 12.08.2019
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Year of Publication 12.08.2019
Patent
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY FOR MUSCULAR DYSTROPHIES
POTTER Rachael, RODINO-KLAPAC Louise, GRIFFIN Danielle, PETERSON Ellyn, MENDELL Jerry R
Year of Publication 03.04.2023
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Year of Publication 03.04.2023
Patent
ADENO-ASSOCIATED VIRUS VECTOR FOR DWARF OPEN READING FRAME
BASSEL-DUBY Rhonda S, OLSON Eric N, MAKAREWICH Catherine A, NELSON Benjamin R
Year of Publication 09.02.2023
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Year of Publication 09.02.2023
Patent
ADENO-ASSOCIATED VIRUS VECTOR PHARMACEUTICAL COMPOSITION AND METHODS
BEE Jared, MARSHALL Tristan, ZHANG Yu, DEPAZ Roberto, O''BERRY Kristin
Year of Publication 19.09.2022
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Year of Publication 19.09.2022
Patent
ADENO ASSOCIATED VIRUS BASED GENE THERAPY FOR PHENYLKETONURIA
ROTTENSTEINER Hanspeter, LENGLER Johannes, KLUGMANN Matthias, HORLING Franziska
Year of Publication 10.08.2022
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Year of Publication 10.08.2022
Patent
PHARMACEUTICAL COMPOSITION COMPRISING A RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR WITH AN EXPRESSION CASSETTE ENCODING A TRANSGENE FORSUPRACHOIDAL ADMINISTRATION
BEE Jared, MARSHALL Tristan James, PAKOLA Stephen Joseph, I YOO Jesse, BUDZYNSKI Ewa, BUSS Nicholas Alexander Piers Sascha, O'BERRY Anthony Ray, EVEREN Sherri Van
Year of Publication 06.12.2024
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Year of Publication 06.12.2024
Patent
MODIFIED ADENO-ASSOCIATED VIRUS (AAV) PARTICLES FOR GENE THERAPY
MAFFEI Mariano, DE CASTRO REIS Fernanda, HEPPENSTALL Paul, POUW Kanyn Morris
Year of Publication 22.02.2022
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Year of Publication 22.02.2022
Patent
Human Treg responses allow sustained recombinant adeno-associated virus–mediated transgene expression
Mueller, Christian, Chulay, Jeffrey D., Trapnell, Bruce C., Humphries, Margaret, Carey, Brenna, Sandhaus, Robert A., McElvaney, Noel G., Messina, Louis, Tang, Qiushi, Rouhani, Farshid N., Campbell-Thompson, Martha, Fu, Ann Dongtao, Yachnis, Anthony, Knop, David R., Ye, Guo-jie, Brantly, Mark, Calcedo, Roberto, Somanathan, Suryanarayan, Richman, Lee P., Vonderheide, Robert H., Hulme, Maigan A., Brusko, Todd M., Wilson, James M., Flotte, Terence R.
Published in The Journal of clinical investigation (01.12.2013)
Published in The Journal of clinical investigation (01.12.2013)
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Journal Article
Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2
Testa, Francesco, Maguire, Albert M., Rossi, Settimio, Pierce, Eric A., Melillo, Paolo, Marshall, Kathleen, Banfi, Sandro, Surace, Enrico M., Sun, Junwei, Acerra, Carmela, Wright, J. Fraser, Wellman, Jennifer, High, Katherine A., Auricchio, Alberto, Bennett, Jean, Simonelli, Francesca
Published in Ophthalmology (Rochester, Minn.) (01.06.2013)
Published in Ophthalmology (Rochester, Minn.) (01.06.2013)
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Journal Article