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Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study
Hewamadduma, Channa, Hinton, John, Juntas-Morales, Raul, Mantegazza, Renato, Sivakumar, Kumaraswamy, Śmiłowski, Marek, Utsugisawa, Kimiaki, Vu, Tuan, Weiss, Michael D, Brock, Melissa, Vanderkelen, Mark, Sembinelli, Dylan, Teitelbaum, Jeanne, Bernard, Emilien, Svahn, Juliette, Stojkovic, Tanya, Demeret, Sophie, Tranchant, Christine, Nadaj-Pakleza, Aleksandra, Chanson, Jean-Baptiste, Lecointe, Peggy, Schmidt, Jens, Zeng, Rachel, Kowarik, Markus, Ziemann, Ulf, Krumbholz, Markus, Martin, Pascal, Dünschede, Jutta, Berger, Benjamin, Stolte, Benjamin, Iorio, Raffaele, Falso, Silvia, Antozzi, Carlo, Frangiamore, Rita, Vanoli, Fiammetta, Rinaldi, Elena, Deguchi, Kazushi, Ishida, Sayaka, Suzuki, Shigeaki, Nakahara, Jin, Nagaoka, Astushi, Uzawa, Akiyuki, Kubota, Tomoya, Takahashi, Masanori, Okuno, Tatsusada, Murai, Hiroyuki, Chyrchel-Paszkiewicz, Urszula, Kumor, Klaudiusz, Błaż, Michał, Szczudlik, Andrzej, Paśko, Aneta, Szczechowski, Lech, Ilkowski, Jan, Kapetanovic Garcia, Solange, Ortiz Bagan, Patricia, Belén Cánovas Segura, Ana, Cortes Vicente, Elena, Rodrigo Armenteros, Patricia, Cavey, Ana, Liow, Kore, Barboi, Alexandru, Guingrich, Sandra, Saba, Sami, Tellez, Marco, Elsheikh, Bakri, Freimer, Miriam, Govindarajan, Raghav, Habib, Ali A, Korb, Manisha, Machemehl, Hannah, Allen, Jeffrey, Harper, Emily, Farmakidis, Constantine, Saavedra, Lilli, Dimachkie, Mazen, McIlduff, Courtney, Barnes, Benjamin, Suresh, Niraja, Shaw, Jessica, Chopra, Manisha, Traub, Rebecca E, Jones, Sarah, Wagoner, Mary, Katz, Jonathan, Jenkins, Liberty, Khan, Shaida, Khatri, Bhupendra, Li, Yuebing, Caristo, Irys B, Rube, Jacob, Lisak, Robert P, Choudhury, Aparna, Ruzhansky, Katherine, Sachdev, Amit, Shin, Susan, Fetter, Mary, McKinnon, Jonathan, Sissons-Ross, Laura, Sahu, Amos, Distad, B Jane
Published in Lancet neurology (01.05.2023)
Published in Lancet neurology (01.05.2023)
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Journal Article
Downregulation of miR-335-5P in Amyotrophic Lateral Sclerosis Can Contribute to Neuronal Mitochondrial Dysfunction and Apoptosis
De Luna, Noemi, Turon-Sans, Joana, Cortes-Vicente, Elena, Carrasco-Rozas, Ana, Illán-Gala, Ignacio, Dols-Icardo, Oriol, Clarimón, Jordi, Lleó, Alberto, Gallardo, Eduard, Illa, Isabel, Rojas-García, Ricardo
Published in Scientific reports (09.03.2020)
Published in Scientific reports (09.03.2020)
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Journal Article