Vyzkoušejte nový nástroj s podporou AI
Summon Research Assistant
BETA
Nuclear architecture dictates HIV-1 integration site selection
Marini, Bruna, Kertesz-Farkas, Attila, Ali, Hashim, Lucic, Bojana, Lisek, Kamil, Manganaro, Lara, Pongor, Sandor, Luzzati, Roberto, Recchia, Alessandra, Mavilio, Fulvio, Giacca, Mauro, Lusic, Marina
Published in Nature (London) (14.05.2015)
Published in Nature (London) (14.05.2015)
Get full text
Journal Article
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements
Lattanzi, Annalisa, Meneghini, Vasco, Pavani, Giulia, Amor, Fatima, Ramadier, Sophie, Felix, Tristan, Antoniani, Chiara, Masson, Cecile, Alibeu, Olivier, Lee, Ciaran, Porteus, Matthew H., Bao, Gang, Amendola, Mario, Mavilio, Fulvio, Miccio, Annarita
Published in Molecular therapy (02.01.2019)
Published in Molecular therapy (02.01.2019)
Get full text
Journal Article
Interactions between Retroviruses and the Host Cell Genome
Poletti, Valentina, Mavilio, Fulvio
Published in Molecular therapy. Methods & clinical development (16.03.2018)
Published in Molecular therapy. Methods & clinical development (16.03.2018)
Get full text
Journal Article
Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity
Eggers, Michelle, Vannoy, Charles H, Huang, Jianyong, Purushothaman, Pravinkumar, Brassard, Jacqueline, Fonck, Carlos, Meng, Hui, Prom, Mariah J, Lawlor, Michael W, Cunningham, Justine, Sadhu, Chanchal, Mavilio, Fulvio
Published in EMBO molecular medicine (11.01.2022)
Published in EMBO molecular medicine (11.01.2022)
Get full text
Journal Article
Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication
Di Nunzio, Francesca, Fricke, Thomas, Miccio, Annarita, Valle-Casuso, Jose Carlos, Perez, Patricio, Souque, Philippe, Rizzi, Ermanno, Severgnini, Marco, Mavilio, Fulvio, Charneau, Pierre, Diaz-Griffero, Felipe
Published in Virology (New York, N.Y.) (25.05.2013)
Published in Virology (New York, N.Y.) (25.05.2013)
Get full text
Journal Article
Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts
Moiani, Arianna, Paleari, Ylenia, Sartori, Daniela, Mezzadra, Riccardo, Miccio, Annarita, Cattoglio, Claudia, Cocchiarella, Fabienne, Lidonnici, Maria Rosa, Ferrari, Giuliana, Mavilio, Fulvio
Published in The Journal of clinical investigation (01.05.2012)
Published in The Journal of clinical investigation (01.05.2012)
Get full text
Journal Article
Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells
Mavilio, Fulvio, Pellegrini, Graziella, Ferrari, Stefano, Di Nunzio, Francesca, Di Iorio, Enzo, Recchia, Alessandra, Maruggi, Giulietta, Ferrari, Giuliana, Provasi, Elena, Bonini, Chiara, Capurro, Sergio, Conti, Andrea, Magnoni, Cristina, Giannetti, Alberto, De Luca, Michele
Published in Nature Medicine (01.12.2006)
Published in Nature Medicine (01.12.2006)
Get full text
Journal Article
Magazine Article
Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed Repair
Izmiryan, Araksya, Ganier, Clarisse, Bovolenta, Matteo, Schmitt, Alain, Mavilio, Fulvio, Hovnanian, Alain
Published in Molecular therapy. Nucleic acids (07.09.2018)
Published in Molecular therapy. Nucleic acids (07.09.2018)
Get full text
Journal Article
Hot spots of retroviral integration in human CD34+ hematopoietic cells
Cattoglio, Claudia, Facchini, Giulia, Sartori, Daniela, Antonelli, Antonella, Miccio, Annarita, Cassani, Barbara, Schmidt, Manfred, von Kalle, Christof, Howe, Steve, Thrasher, Adrian J., Aiuti, Alessandro, Ferrari, Giuliana, Recchia, Alessandra, Mavilio, Fulvio
Published in Blood (15.09.2007)
Published in Blood (15.09.2007)
Get full text
Journal Article
Correction: Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells
Turchiano, Giandomenico, Latella, Maria Carmela, Döring, Andreas Gogol, Cattoglio, Claudia, Mavilio, Fulvio, Izsvák, Zsuzsanna, Ivics, Zoltán, Recchia, Alessandra
Published in PloS one (30.01.2020)
Published in PloS one (30.01.2020)
Get full text
Journal Article
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies
Brusson, Mégane, Chalumeau, Anne, Martinucci, Pierre, Romano, Oriana, Felix, Tristan, Poletti, Valentina, Scaramuzza, Samantha, Ramadier, Sophie, Masson, Cecile, Ferrari, Giuliana, Mavilio, Fulvio, Cavazzana, Marina, Amendola, Mario, Miccio, Annarita
Published in Molecular therapy. Nucleic acids (13.06.2023)
Published in Molecular therapy. Nucleic acids (13.06.2023)
Get full text
Journal Article
Cerebellar Pathology in an Inducible Mouse Model of Friedreich Ataxia
Mercado-Ayón, Elizabeth, Warren, Nathan, Halawani, Sarah, Rodden, Layne N., Ngaba, Lucie, Dong, Yi Na, Chang, Joshua C., Fonck, Carlos, Mavilio, Fulvio, Lynch, David R., Lin, Hong
Published in Frontiers in neuroscience (24.03.2022)
Published in Frontiers in neuroscience (24.03.2022)
Get full text
Journal Article
Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells
Turchiano, Giandomenico, Latella, Maria Carmela, Gogol-Döring, Andreas, Cattoglio, Claudia, Mavilio, Fulvio, Izsvák, Zsuzsanna, Ivics, Zoltán, Recchia, Alessandra
Published in PloS one (12.11.2014)
Published in PloS one (12.11.2014)
Get full text
Journal Article
Transcription Factor Binding Sites Are Genetic Determinants of Retroviral Integration in the Human Genome
Felice, Barbara, Cattoglio, Claudia, Cittaro, Davide, Testa, Anna, Miccio, Annarita, Ferrari, Giuliana, Luzi, Lucilla, Recchia, Alessandra, Mavilio, Fulvio
Published in PloS one (24.02.2009)
Published in PloS one (24.02.2009)
Get full text
Journal Article
Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System
Lattanzi, Annalisa, Duguez, Stephanie, Moiani, Arianna, Izmiryan, Araksya, Barbon, Elena, Martin, Samia, Mamchaoui, Kamel, Mouly, Vincent, Bernardi, Francesco, Mavilio, Fulvio, Bovolenta, Matteo
Published in Molecular therapy. Nucleic acids (16.06.2017)
Published in Molecular therapy. Nucleic acids (16.06.2017)
Get full text
Journal Article
Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination
Coluccio, Andrea, Miselli, Francesca, Lombardo, Angelo, Marconi, Alessandra, Malagoli Tagliazucchi, Guidantonio, Gonçalves, Manuel A, Pincelli, Carlo, Maruggi, Giulietta, Del Rio, Marcela, Naldini, Luigi, Larcher, Fernando, Mavilio, Fulvio, Recchia, Alessandra
Published in Molecular therapy (01.09.2013)
Published in Molecular therapy (01.09.2013)
Get full text
Journal Article
The Pharmacology of Gene and Cell Therapy
Conlon, Thomas J., Mavilio, Fulvio
Published in Molecular therapy. Methods & clinical development (16.03.2018)
Published in Molecular therapy. Methods & clinical development (16.03.2018)
Get full text
Journal Article
Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency
Poletti, Valentina, Charrier, Sabine, Corre, Guillaume, Gjata, Bernard, Vignaud, Alban, Zhang, Fang, Rothe, Michael, Schambach, Axel, Gaspar, H. Bobby, Thrasher, Adrian J., Mavilio, Fulvio
Published in Molecular therapy. Methods & clinical development (15.06.2018)
Published in Molecular therapy. Methods & clinical development (15.06.2018)
Get full text
Journal Article
Muscle-Derived Hematopoietic Stem Cells are Hematopoietic in Origin
McKinney-Freeman, Shannon L., Jackson, Kathyjo A., Camargo, Fernando D., Ferrari, Giuliana, Mavilio, Fulvio, Goodell, Margaret A.
Published in Proceedings of the National Academy of Sciences - PNAS (05.02.2002)
Published in Proceedings of the National Academy of Sciences - PNAS (05.02.2002)
Get full text
Journal Article