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COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa
Hainzl, Stefan, Peking, Patricia, Kocher, Thomas, Murauer, Eva M., Larcher, Fernando, Del Rio, Marcela, Duarte, Blanca, Steiner, Markus, Klausegger, Alfred, Bauer, Johann W., Reichelt, Julia, Koller, Ulrich
Published in Molecular therapy (01.11.2017)
Published in Molecular therapy (01.11.2017)
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Journal Article
Functional therapies for cutaneous wound repair in epidermolysis bullosa
Peking, Patricia, Koller, Ulrich, Murauer, Eva M.
Published in Advanced drug delivery reviews (01.04.2018)
Published in Advanced drug delivery reviews (01.04.2018)
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Journal Article
QR-313, an Antisense Oligonucleotide, Shows Therapeutic Efficacy for Treatment of Dominant and Recessive Dystrophic Epidermolysis Bullosa: A Preclinical Study
Bornert, Olivier, Hogervorst, Marieke, Nauroy, Pauline, Bischof, Johannes, Swildens, Jim, Athanasiou, Ioannis, Tufa, Sara F., Keene, Douglas R., Kiritsi, Dimitra, Hainzl, Stefan, Murauer, Eva M., Marinkovich, M. Peter, Platenburg, Gerard, Hausser, Ingrid, Wally, Verena, Ritsema, Tita, Koller, Ulrich, Haisma, Elisabeth M., Nyström, Alexander
Published in Journal of investigative dermatology (01.04.2021)
Published in Journal of investigative dermatology (01.04.2021)
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Journal Article
Context-Dependent Strategies for Enhanced Genome Editing of Genodermatoses
March, Oliver Patrick, Kocher, Thomas, Koller, Ulrich
Published in Cells (Basel, Switzerland) (02.01.2020)
Published in Cells (Basel, Switzerland) (02.01.2020)
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Journal Article
Transmission electron microscopy of dermal collagen using ethanolic phosphotungstic acid staining
Obermayer, Astrid, Hainzl, Stefan, Koller, Ulrich, Stoiber, Walter
Published in BIO web of conferences (2024)
Published in BIO web of conferences (2024)
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Journal Article
Conference Proceeding
Traceless Targeting and Isolation of Gene-Edited Immortalized Keratinocytes from Epidermolysis Bullosa Simplex Patients
Aushev, Magomet, Koller, Ulrich, Mussolino, Claudio, Cathomen, Toni, Reichelt, Julia
Published in Molecular therapy. Methods & clinical development (15.09.2017)
Published in Molecular therapy. Methods & clinical development (15.09.2017)
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Journal Article
Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination
Kocher, Thomas, Wagner, Roland N., Klausegger, Alfred, Guttmann-Gruber, Christina, Hainzl, Stefan, Bauer, Johann W., Reichelt, Julia, Koller, Ulrich
Published in Molecular therapy. Nucleic acids (06.12.2019)
Published in Molecular therapy. Nucleic acids (06.12.2019)
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Journal Article
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa
Kocher, Thomas, Bischof, Johannes, Haas, Simone Alexandra, March, Oliver Patrick, Liemberger, Bernadette, Hainzl, Stefan, Illmer, Julia, Hoog, Anna, Muigg, Katharina, Binder, Heide-Marie, Klausegger, Alfred, Strunk, Dirk, Bauer, Johann Wolfgang, Cathomen, Toni, Koller, Ulrich
Published in Molecular therapy. Nucleic acids (03.09.2021)
Published in Molecular therapy. Nucleic acids (03.09.2021)
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Journal Article
Evaluating a Targeted Cancer Therapy Approach Mediated by RNA trans-Splicing In Vitro and in a Xenograft Model for Epidermolysis Bullosa-Associated Skin Cancer
Woess, Katharina, Sun, Yuchen, Morio, Hanae, Stierschneider, Anna, Kaufmann, Anna, Hainzl, Stefan, Trattner, Lisa, Kocher, Thomas, Tockner, Birgit, Leb-Reichl, Victoria, Steiner, Markus, Brachtl, Gabriele, South, Andrew P, Bauer, Johann W, Reichelt, Julia, Furihata, Tomomi, Wally, Verena, Koller, Ulrich, Piñón Hofbauer, Josefina, Guttmann-Gruber, Christina
Published in International Journal of Molecular Sciences (05.01.2022)
Published in International Journal of Molecular Sciences (05.01.2022)
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Journal Article
Cancer-type organic anion transporting polypeptide 1B3 is a target for cancer suicide gene therapy using RNA trans-splicing technology
Sun, Yuchen, Piñón Hofbauer, Josefina, Harada, Manami, Wöss, Katharina, Koller, Ulrich, Morio, Hanae, Stierschneider, Anna, Kitamura, Keita, Hashimoto, Mari, Chiba, Kan, Akita, Hidetaka, Anzai, Naohiko, Reichelt, Julia, Bauer, Johann W., Guttmann-Gruber, Christina, Furihata, Tomomi
Published in Cancer letters (01.10.2018)
Published in Cancer letters (01.10.2018)
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Journal Article
RNA Trans-Splicing Modulation via Antisense Molecule Interference
Liemberger, Bernadette, Piñón Hofbauer, Josefina, Wally, Verena, Arzt, Claudia, Hainzl, Stefan, Kocher, Thomas, Murauer, Eva, Bauer, Johann, Reichelt, Julia, Koller, Ulrich
Published in International journal of molecular sciences (07.03.2018)
Published in International journal of molecular sciences (07.03.2018)
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Journal Article
COL17A1 editing via homology-directed repair in junctional epidermolysis bullosa
Petković, Igor, Bischof, Johannes, Kocher, Thomas, March, Oliver Patrick, Liemberger, Bernadette, Hainzl, Stefan, Strunk, Dirk, Raninger, Anna Maria, Binder, Heide-Marie, Reichelt, Julia, Guttmann-Gruber, Christina, Wally, Verena, Piñón Hofbauer, Josefina, Bauer, Johann Wolfgang, Koller, Ulrich
Published in Frontiers in medicine (25.08.2022)
Published in Frontiers in medicine (25.08.2022)
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Journal Article
Generation of rabbit polyclonal human and murine collagen VII monospecific antibodies: A useful tool for dystrophic epidermolysis bullosa therapy studies
Bornert, Olivier, Kocher, Thomas, Gretzmeier, Christine, Liemberger, Bernadette, Hainzl, Stefan, Koller, Ulrich, Nyström, Alexander
Published in Matrix biology plus (01.11.2019)
Published in Matrix biology plus (01.11.2019)
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Journal Article
Advances in Gene/Cell Therapy in Epidermolysis Bullosa
Koller, Ulrich, luca, Michele De, Pellegrini, Graziella, Bauer, Johann W., Murauer, Eva M.
Published in Keio journal of medicine (2015)
Published in Keio journal of medicine (2015)
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Journal Article
A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair
Peking, Patricia, Koller, Ulrich, Hainzl, Stefan, Kitzmueller, Sophie, Kocher, Thomas, Mayr, Elisabeth, Nyström, Alexander, Lener, Thomas, Reichelt, Julia, Bauer, Johann W, Murauer, Eva M
Published in Molecular therapy. Nucleic acids (01.03.2016)
Published in Molecular therapy. Nucleic acids (01.03.2016)
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Journal Article