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Propensity score matching and inverse probability of treatment weighting to address confounding by indication in comparative effectiveness research of oral anticoagulants
Allan, Victoria, Ramagopalan, Sreeram V, Mardekian, Jack, Jenkins, Aaron, Li, Xiaoyan, Pan, Xianying, Luo, Xuemei
Published in Journal of comparative effectiveness research (01.06.2020)
Published in Journal of comparative effectiveness research (01.06.2020)
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Journal Article
Efficacy classification of modern therapies in multiple sclerosis
Samjoo, Imtiaz A, Worthington, Evelyn, Drudge, Christopher, Zhao, Melody, Cameron, Chris, Häring, Dieter A, Stoneman, Dee, Klotz, Luisa, Adlard, Nicholas
Published in Journal of comparative effectiveness research (01.04.2021)
Published in Journal of comparative effectiveness research (01.04.2021)
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Journal Article
Comparison of weighting methods used in multicriteria decision analysis frameworks in healthcare with focus on low- and middle-income countries
Németh, Bertalan, Molnár, Anett, Bozóki, Sándor, Wijaya, Kalman, Inotai, András, Campbell, Jonathan D, Kaló, Zoltán
Published in Journal of comparative effectiveness research (01.03.2019)
Published in Journal of comparative effectiveness research (01.03.2019)
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Journal Article
Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study
Mercuri, Eugenio, Muntoni, Francesco, Osorio, Andrés Nascimento, Tulinius, Már, Buccella, Filippo, Morgenroth, Lauren P, Gordish-Dressman, Heather, Jiang, Joel, Trifillis, Panayiota, Zhu, Jin, Kristensen, Allan, Santos, Claudio L, Henricson, Erik K, McDonald, Craig M, Desguerre, Isabelle
Published in Journal of comparative effectiveness research (01.04.2020)
Published in Journal of comparative effectiveness research (01.04.2020)
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Journal Article
Evaluating patient and stakeholder engagement in research: moving from theory to practice
Esmail, Laura, Moore, Emily, Rein, Alison
Published in Journal of comparative effectiveness research (01.03.2015)
Published in Journal of comparative effectiveness research (01.03.2015)
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Journal Article
Framework and guidance for implementing patient-reported outcomes in clinical practice: evidence, challenges and opportunities
Porter, Ian, Gonçalves-Bradley, Daniela, Ricci-Cabello, Ignacio, Gibbons, Chris, Gangannagaripalli, Jaheeda, Fitzpatrick, Ray, Black, Nick, Greenhalgh, Joanne, Valderas, Jose M
Published in Journal of comparative effectiveness research (01.08.2016)
Published in Journal of comparative effectiveness research (01.08.2016)
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Journal Article
Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients
McDonald, Craig M, Muntoni, Francesco, Penematsa, Vinay, Jiang, Joel, Kristensen, Allan, Bibbiani, Francesco, Goodwin, Elizabeth, Gordish-Dressman, Heather, Morgenroth, Lauren, Werner, Christian, Li, James, Able, Richard, Trifillis, Panayiota, Tulinius, Már, Ryan, M, Jones, K, Goemans, N, Campbell, C, Mah, JK, Selby, K, Chabrol, B, Pereon, Y, Voit, T, Gidaro, T, Schara, U, Kirschner, JB, Nevo, Y, Comi, GP, Bertini, E, Mercuri, E, Colomer, J, Nascimento, A, Vilchez, JJ, Tulinius, M, Sejersen, T, Muntoni, F, Bushby, K, Guglieri, M
Published in Journal of comparative effectiveness research (01.02.2022)
Published in Journal of comparative effectiveness research (01.02.2022)
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Journal Article
COVID-19 complications in males and females: recent developments
Chaturvedi, Rahul, Lui, Briana, Aaronson, Jamie A, White, Robert S, Samuels, Jon D
Published in Journal of comparative effectiveness research (01.06.2022)
Published in Journal of comparative effectiveness research (01.06.2022)
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Journal Article
Comparison of ofatumumab and other disease-modifying therapies for relapsing multiple sclerosis: a network meta-analysis
Samjoo, Imtiaz A, Worthington, Evelyn, Drudge, Christopher, Zhao, Melody, Cameron, Chris, Häring, Dieter A, Stoneman, Dee, Klotz, Luisa, Adlard, Nicholas
Published in Journal of comparative effectiveness research (01.12.2020)
Published in Journal of comparative effectiveness research (01.12.2020)
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Journal Article
Organized structure of real-world evidence best practices: moving from fragmented recommendations to comprehensive guidance
Jaksa, Ashley, Wu, James, Jónsson, Páll, Eichler, Hans-Georg, Vititoe, Sarah, Gatto, Nicolle M
Published in Journal of comparative effectiveness research (01.06.2021)
Published in Journal of comparative effectiveness research (01.06.2021)
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Journal Article
Comparative efficacy of therapies for relapsing multiple sclerosis: a systematic review and network meta-analysis
Samjoo, Imtiaz A, Drudge, Christopher, Walsh, Sarah, Tiwari, Santosh, Brennan, Róisín, Boer, Ibolya, Häring, Dieter A, Klotz, Luisa, Adlard, Nicholas, Banhazi, Judit
Published in Journal of comparative effectiveness research (01.07.2023)
Published in Journal of comparative effectiveness research (01.07.2023)
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Journal Article
Navigating adalimumab biosimilars: an expert opinion
Abitbol, Vered, Benkhalifa, Salim, Habauzit, Caroline, Marotte, Hubert
Published in Journal of comparative effectiveness research (01.11.2023)
Published in Journal of comparative effectiveness research (01.11.2023)
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Journal Article
How does risdiplam compare with other treatments for Types 1–3 spinal muscular atrophy: a systematic literature review and indirect treatment comparison
Ribero, Valerie Aponte, Daigl, Monica, Martí, Yasmina, Gorni, Ksenija, Evans, Rachel, Scott, David Alexander, Mahajan, Anadi, Abrams, Keith R, Hawkins, Neil
Published in Journal of comparative effectiveness research (01.04.2022)
Published in Journal of comparative effectiveness research (01.04.2022)
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Journal Article
Safety and effectiveness of intranasal esketamine for treatment-resistant depression: a real-world retrospective study
Brendle, Madeline, Ahuja, Sachin, Valle, Maisa Della, Moore, Claire, Thielking, Paul, Malone, Daniel C, Robison, Reid
Published in Journal of comparative effectiveness research (01.12.2022)
Published in Journal of comparative effectiveness research (01.12.2022)
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Journal Article
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Campbell, Craig, Barohn, Richard J, Bertini, Enrico, Chabrol, Brigitte, Comi, Giacomo Pietro, Darras, Basil T, Finkel, Richard S, Flanigan, Kevin M, Goemans, Nathalie, Iannaccone, Susan T, Jones, Kristi J, Kirschner, Janbernd, Mah, Jean K, Mathews, Katherine D, McDonald, Craig M, Mercuri, Eugenio, Nevo, Yoram, Péréon, Yann, Renfroe, J Ben, Ryan, Monique M, Sampson, Jacinda B, Schara, Ulrike, Sejersen, Thomas, Selby, Kathryn, Tulinius, Már, Vílchez, Juan J, Voit, Thomas, Wei, Lee-Jen, Wong, Brenda L, Elfring, Gary, Souza, Marcio, McIntosh, Joseph, Trifillis, Panayiota, Peltz, Stuart W, Muntoni, Francesco
Published in Journal of comparative effectiveness research (01.10.2020)
Published in Journal of comparative effectiveness research (01.10.2020)
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Journal Article
Evidence-based public policy making for medicines across countries: findings and implications for the future
Godman, Brian, Fadare, Joseph, Kwon, Hye-Young, Dias, Carolina Zampirolli, Kurdi, Amanj, Dias Godói, Isabella Piassi, Kibuule, Dan, Hoxha, Iris, Opanga, Sylvia, Saleem, Zikria, Bochenek, Tomasz, Marković-Peković, Vanda, Mardare, Ileana, Kalungia, Aubrey C, Campbell, Stephen, Allocati, Eleonora, Pisana, Alice, Martin, Antony P, Meyer, Johanna C
Published in JOURNAL OF COMPARATIVE EFFECTIVENESS RESEARCH (01.08.2021)
Published in JOURNAL OF COMPARATIVE EFFECTIVENESS RESEARCH (01.08.2021)
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