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Repurposing diacerein for the treatment of chronic wounds in recessive‐dystrophic epidermolysis bullosa patients by modulating matrix metalloproteinase‐9 expression
Dorfer, Sonja, Ablinger, Michael, Wimmer, Monika, Hummel, Julia I., Ibrahimpašić, Selma, Diem, Anja, Laimer, Martin, Gruner, Stefanie, Hofbauer, Josefina Piñón, Guttmann‐Gruber, Christina, Koller, Ulrich, Gratz, Iris K., Bauer, Johann W., Zauner, Roland, Wally, Verena
Published in Journal of dermatology (01.03.2025)
Published in Journal of dermatology (01.03.2025)
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Journal Article
5′RNA Trans-Splicing Repair of COL7A1 Mutant Transcripts in Epidermolysis Bullosa
Mayr, Elisabeth, Ablinger, Michael, Lettner, Thomas, Murauer, Eva M., Guttmann-Gruber, Christina, Piñón Hofbauer, Josefina, Hainzl, Stefan, Kaiser, Manfred, Klausegger, Alfred, Bauer, Johann W., Koller, Ulrich, Wally, Verena
Published in International journal of molecular sciences (01.02.2022)
Published in International journal of molecular sciences (01.02.2022)
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Journal Article
Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination
Kocher, Thomas, Wagner, Roland N., Klausegger, Alfred, Guttmann-Gruber, Christina, Hainzl, Stefan, Bauer, Johann W., Reichelt, Julia, Koller, Ulrich
Published in Molecular therapy. Nucleic acids (06.12.2019)
Published in Molecular therapy. Nucleic acids (06.12.2019)
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Journal Article
Impact of low-dose calcipotriol ointment on wound healing, pruritus and pain in patients with dystrophic epidermolysis bullosa: A randomized, double-blind, placebo-controlled trial
Guttmann-Gruber, Christina, Piñón Hofbauer, Josefina, Tockner, Birgit, Reichl, Victoria, Klausegger, Alfred, Hofbauer, Peter, Wolkersdorfer, Martin, Tham, Khek-Chian, Lim, Seong Soo, Common, John E., Diem, Anja, Ude-Schoder, Katharina, Hitzl, Wolfgang, Lagler, Florian, Reichelt, Julia, Bauer, Johann W., Lang, Roland, Laimer, Martin
Published in Orphanet journal of rare diseases (08.11.2021)
Published in Orphanet journal of rare diseases (08.11.2021)
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Journal Article
Induced pluripotent stem cell (iPSC) line MLi005-A derived from a patient with dominant dystrophic epidermolysis bullosa (DDEB)
Ropret, Sandra, Khurana, Preeti, Fabčič, Tara, Cvetkovska, Janina, Trobec, Ana, Jokhadar, Špela Zemljič, Ilic, Dusko, McGrath, John A, Guttmann-Gruber, Christina, Liovic, Mirjana
Published in Stem cell research (01.03.2024)
Published in Stem cell research (01.03.2024)
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Journal Article
Evaluating a Targeted Cancer Therapy Approach Mediated by RNA trans-Splicing In Vitro and in a Xenograft Model for Epidermolysis Bullosa-Associated Skin Cancer
Woess, Katharina, Sun, Yuchen, Morio, Hanae, Stierschneider, Anna, Kaufmann, Anna, Hainzl, Stefan, Trattner, Lisa, Kocher, Thomas, Tockner, Birgit, Leb-Reichl, Victoria, Steiner, Markus, Brachtl, Gabriele, South, Andrew P, Bauer, Johann W, Reichelt, Julia, Furihata, Tomomi, Wally, Verena, Koller, Ulrich, Piñón Hofbauer, Josefina, Guttmann-Gruber, Christina
Published in International Journal of Molecular Sciences (05.01.2022)
Published in International Journal of Molecular Sciences (05.01.2022)
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Journal Article
Cancer-type organic anion transporting polypeptide 1B3 is a target for cancer suicide gene therapy using RNA trans-splicing technology
Sun, Yuchen, Piñón Hofbauer, Josefina, Harada, Manami, Wöss, Katharina, Koller, Ulrich, Morio, Hanae, Stierschneider, Anna, Kitamura, Keita, Hashimoto, Mari, Chiba, Kan, Akita, Hidetaka, Anzai, Naohiko, Reichelt, Julia, Bauer, Johann W., Guttmann-Gruber, Christina, Furihata, Tomomi
Published in Cancer letters (01.10.2018)
Published in Cancer letters (01.10.2018)
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Journal Article
A cancer stem cell-like phenotype is associated with miR-10b expression in aggressive squamous cell carcinomas
Wimmer, Monika, Zauner, Roland, Ablinger, Michael, Piñón-Hofbauer, Josefina, Guttmann-Gruber, Christina, Reisenberger, Manuela, Lettner, Thomas, Niklas, Norbert, Proell, Johannes, Sajinovic, Mila, De Souza, Paul, Hainzl, Stefan, Kocher, Thomas, Murauer, Eva M., Bauer, Johann W., Strunk, Dirk, Reichelt, Julia, Mellick, Albert Sleiman, Wally, Verena
Published in Cell communication and signaling (10.04.2020)
Published in Cell communication and signaling (10.04.2020)
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Journal Article
Extracellular Vesicles as Biomarkers for the Detection of a Tumor Marker Gene in Epidermolysis Bullosa-Associated Squamous Cell Carcinoma
Sun, Yuchen, Woess, Katharina, Kienzl, Melanie, Leb-Reichl, Victoria M., Feinle, Andrea, Wimmer, Monika, Zauner, Roland, Wally, Verena, Luetz-Meindl, Ursula, Mellerio, Jemima E., Fuentes, Ignacia, South, Andrew P., Bauer, Johann W., Reichelt, Julia, Furihata, Tomomi, Guttmann-Gruber, Christina, Piñón Hofbauer, Josefina
Published in Journal of investigative dermatology (01.05.2018)
Published in Journal of investigative dermatology (01.05.2018)
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Journal Article
COL17A1 editing via homology-directed repair in junctional epidermolysis bullosa
Petković, Igor, Bischof, Johannes, Kocher, Thomas, March, Oliver Patrick, Liemberger, Bernadette, Hainzl, Stefan, Strunk, Dirk, Raninger, Anna Maria, Binder, Heide-Marie, Reichelt, Julia, Guttmann-Gruber, Christina, Wally, Verena, Piñón Hofbauer, Josefina, Bauer, Johann Wolfgang, Koller, Ulrich
Published in Frontiers in medicine (25.08.2022)
Published in Frontiers in medicine (25.08.2022)
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Journal Article
Cancer-Type OATP1B3 mRNA in Extracellular Vesicles as a Promising Candidate for a Serum-Based Colorectal Cancer Biomarker
Yamaguchi, Naoto, Sun, Yuchen, Zhou, Xujia, Morio, Hanae, Furihata, Tomomi, Shimozato, Osamu, Anzai, Naohiko, Harada, Manami, Ide, Hideyuki, Yuki, Ryuzaburo, Higashi, Kenjirou, Akita, Hidetaka, Hofbauer, Josefina Piñón, Chiba, Kan, Guttmann-Gruber, Christina
Published in Biological & pharmaceutical bulletin (2018)
Published in Biological & pharmaceutical bulletin (2018)
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Journal Article
Leveraging immune memory against measles virus as an antitumor strategy in a preclinical model of aggressive squamous cell carcinoma
Leb-Reichl, Victoria M, Kienzl, Melanie, Kaufmann, Anna, Stoecklinger, Angelika, Tockner, Birgit, Kitzmueller, Sophie, Zaborsky, Nadja, Steiner, Markus, Brachtl, Gabriele, Trattner, Lisa, Kreideweiss, Patrick, Reinsch, Christian, Panzner, Steffen, Greil, Richard, Strunk, Dirk, Bauer, Johann W, Gratz, Iris K, Guttmann-Gruber, Christina, Piñón Hofbauer, Josefina
Published in Journal for immunotherapy of cancer (01.10.2021)
Published in Journal for immunotherapy of cancer (01.10.2021)
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Journal Article
Challenges and progress related to gene editing in rare skin diseases
Piñón Hofbauer, Josefina, Guttmann-Gruber, Christina, Wally, Verena, Sharma, Anshu, Gratz, Iris K., Koller, Ulrich
Published in Advanced drug delivery reviews (01.05.2024)
Published in Advanced drug delivery reviews (01.05.2024)
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Journal Article
Thrombospondin-1 Is a Major Activator of TGF-β Signaling in Recessive Dystrophic Epidermolysis Bullosa Fibroblasts
Atanasova, Velina S., Russell, Rebecca J., Webster, Timothy G., Cao, Qingqing, Agarwal, Pooja, Lim, Yok Zuan, Krishnan, Suma, Fuentes, Ignacia, Guttmann-Gruber, Christina, McGrath, John A., Salas-Alanis, Julio C., Fertala, Andrzej, South, Andrew P.
Published in Journal of investigative dermatology (01.07.2019)
Published in Journal of investigative dermatology (01.07.2019)
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Journal Article
NETSKINMODELS: A European Network for Skin Engineering and Modeling
Goreski, Hristijan, Ilic, Dusko, Flacher, Vincent, van den Bogaard, Ellen, Guttmann-Gruber, Christina, Tanaka, Reiko J., Gülseren, Gülcihan, Marquette, Christophe, Fluhr, Joachim, Filor, Viviane, Sprincean, Serghei, Dubrac, Sandrine
Published in Journal of investigative dermatology (01.01.2025)
Published in Journal of investigative dermatology (01.01.2025)
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Journal Article
Gene Editing–Mediated Disruption of Epidermolytic Ichthyosis–Associated KRT10 Alleles Restores Filament Stability in Keratinocytes
March, Oliver P., Lettner, Thomas, Klausegger, Alfred, Ablinger, Michael, Kocher, Thomas, Hainzl, Stefan, Peking, Patricia, Lackner, Nina, Rajan, Neil, Hofbauer, Josefina Piñón, Guttmann-Gruber, Christina, Bygum, Anette, Koller, Ulrich, Reichelt, Julia
Published in Journal of investigative dermatology (01.08.2019)
Published in Journal of investigative dermatology (01.08.2019)
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Journal Article
Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa
Bischof, Johannes, March, Oliver Patrick, Liemberger, Bernadette, Haas, Simone Alexandra, Hainzl, Stefan, Petković, Igor, Leb-Reichl, Victoria, Illmer, Julia, Korotchenko, Evgeniia, Klausegger, Alfred, Hoog, Anna, Binder, Heide-Marie, Garcia, Marta, Duarte, Blanca, Strunk, Dirk, Larcher, Fernando, Reichelt, Julia, Guttmann-Gruber, Christina, Wally, Verena, Hofbauer, Josefina Piñón, Bauer, Johann Wolfgang, Cathomen, Toni, Kocher, Thomas, Koller, Ulrich
Published in Molecular therapy (03.08.2022)
Published in Molecular therapy (03.08.2022)
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Journal Article
MicroRNA-200b-mediated reversion of a spectrum of epithelial-to-mesenchymal transition states in recessive dystrophic epidermolysis bullosa squamous cell carcinomas
Illmer, Julia, Zauner, Roland, Piñón Hofbauer, Josefina, Wimmer, Monika, Gruner, Stefanie, Ablinger, Michael, Bischof, Johannes, Dorfer, Sonja, Hainzl, Stefan, Tober, Vanessa, Bergson, Shir, Sarig, Ofer, Samuelov, Liat, Guttmann-Gruber, Christina, Shalom-Feuerstein, Ruby, Sprecher, Eli, Koller, Ulrich, Laimer, Martin, Bauer, Johann W, Wally, Verena
Published in British journal of dermatology (1951) (20.12.2023)
Published in British journal of dermatology (1951) (20.12.2023)
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Journal Article