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Long non-coding RNAs as novel therapeutic targets in juvenile myelomonocytic leukemia
Hofmans, Mattias, Lammens, Tim, Depreter, Barbara, Wu, Ying, Erlacher, Miriam, Caye, Aurélie, Cavé, Hélène, Flotho, Christian, de Haas, Valerie, Niemeyer, Charlotte M., Stary, Jan, Van Nieuwerburgh, Filip, Deforce, Dieter, Van Loocke, Wouter, Van Vlierberghe, Pieter, Philippé, Jan, De Moerloose, Barbara
Published in Scientific reports (02.02.2021)
Published in Scientific reports (02.02.2021)
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Journal Article
Publisher Correction: Clinical evolution, genetic landscape and trajectories of clonal hematopoiesis in SAMD9/SAMD9L syndromes
Sahoo, Sushree S., Pastor, Victor B., Goodings, Charnise, Voss, Rebecca K., Kozyra, Emilia J., Szvetnik, Amina, Noellke, Peter, Dworzak, Michael, Starý, Jan, Locatelli, Franco, Masetti, Riccardo, Schmugge, Markus, De Moerloose, Barbara, Catala, Albert, Kállay, Krisztián, Turkiewicz, Dominik, Hasle, Henrik, Buechner, Jochen, Jahnukainen, Kirsi, Ussowicz, Marek, Polychronopoulou, Sophia, Smith, Owen P., Fabri, Oksana, Barzilai, Shlomit, de Haas, Valerie, Baumann, Irith, Schwarz-Furlan, Stephan, Niewisch, Marena R., Sauer, Martin G., Burkhardt, Birgit, Lang, Peter, Bader, Peter, Beier, Rita, Müller, Ingo, Albert, Michael H., Meisel, Roland, Schulz, Ansgar, Cario, Gunnar, Panda, Pritam K., Wehrle, Julius, Hirabayashi, Shinsuke, Derecka, Marta, Durruthy-Durruthy, Robert, Göhring, Gudrun, Yoshimi-Noellke, Ayami, Ku, Manching, Lebrecht, Dirk, Erlacher, Miriam, Flotho, Christian, Strahm, Brigitte, Niemeyer, Charlotte M., Wlodarski, Marcin W.
Published in Nature medicine (01.12.2021)
Published in Nature medicine (01.12.2021)
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Deciphering the Non-Coding RNA Landscape of Pediatric Acute Myeloid Leukemia
Vanhooren, Jolien, Van Camp, Laurens, Depreter, Barbara, de Jong, Martijn, Uyttebroeck, Anne, Van Damme, An, Dedeken, Laurence, Dresse, Marie-Françoise, van der Werff ten Bosch, Jutte, Hofmans, Mattias, Philippé, Jan, De Moerloose, Barbara, Lammens, Tim
Published in Cancers (22.04.2022)
Published in Cancers (22.04.2022)
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Genetic mechanisms of target antigen loss in CAR19 therapy of acute lymphoblastic leukemia
Orlando, Elena J, Han, Xia, Tribouley, Catherine, Wood, Patricia A, Leary, Rebecca J, Riester, Markus, Levine, John E, Qayed, Muna, Grupp, Stephan A, Boyer, Michael, De Moerloose, Barbara, Nemecek, Eneida R, Bittencourt, Henrique, Hiramatsu, Hidefumi, Buechner, Jochen, Davies, Stella M, Verneris, Michael R, Nguyen, Kevin, Brogdon, Jennifer L, Bitter, Hans, Morrissey, Michael, Pierog, Piotr, Pantano, Serafino, Engelman, Jeffrey A, Winckler, Wendy
Published in Nature medicine (01.10.2018)
Published in Nature medicine (01.10.2018)
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Journal Article
Clinical evolution, genetic landscape and trajectories of clonal hematopoiesis in SAMD9/SAMD9L syndromes
Sahoo, Sushree S., Pastor, Victor B., Goodings, Charnise, Voss, Rebecca K., Kozyra, Emilia J., Szvetnik, Amina, Noellke, Peter, Dworzak, Michael, Starý, Jan, Locatelli, Franco, Masetti, Riccardo, Schmugge, Markus, De Moerloose, Barbara, Catala, Albert, Kállay, Krisztián, Turkiewicz, Dominik, Hasle, Henrik, Buechner, Jochen, Jahnukainen, Kirsi, Ussowicz, Marek, Polychronopoulou, Sophia, Smith, Owen P., Fabri, Oksana, Barzilai, Shlomit, de Haas, Valerie, Baumann, Irith, Schwarz-Furlan, Stephan, Niewisch, Marena R., Sauer, Martin G., Burkhardt, Birgit, Lang, Peter, Bader, Peter, Beier, Rita, Müller, Ingo, Albert, Michael H., Meisel, Roland, Schulz, Ansgar, Cario, Gunnar, Panda, Pritam K., Wehrle, Julius, Hirabayashi, Shinsuke, Derecka, Marta, Durruthy-Durruthy, Robert, Göhring, Gudrun, Yoshimi-Noellke, Ayami, Ku, Manching, Lebrecht, Dirk, Erlacher, Miriam, Flotho, Christian, Strahm, Brigitte, Niemeyer, Charlotte M., Wlodarski, Marcin W.
Published in Nature medicine (01.10.2021)
Published in Nature medicine (01.10.2021)
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Prevalence, clinical characteristics, and prognosis of GATA2-related myelodysplastic syndromes in children and adolescents
Wlodarski, Marcin W., Hirabayashi, Shinsuke, Pastor, Victor, Starý, Jan, Hasle, Henrik, Masetti, Riccardo, Dworzak, Michael, Schmugge, Markus, van den Heuvel-Eibrink, Marry, Ussowicz, Marek, De Moerloose, Barbara, Catala, Albert, Smith, Owen P., Sedlacek, Petr, Lankester, Arjan C., Zecca, Marco, Bordon, Victoria, Matthes-Martin, Susanne, Abrahamsson, Jonas, Kühl, Jörn Sven, Sykora, Karl-Walter, Albert, Michael H., Przychodzien, Bartlomiej, Maciejewski, Jaroslaw P., Schwarz, Stephan, Göhring, Gudrun, Schlegelberger, Brigitte, Cseh, Annámaria, Noellke, Peter, Yoshimi, Ayami, Locatelli, Franco, Baumann, Irith, Strahm, Brigitte, Niemeyer, Charlotte M.
Published in Blood (17.03.2016)
Published in Blood (17.03.2016)
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Collaborative Efforts Driving Progress in Pediatric Acute Myeloid Leukemia
Zwaan, C. Michel, Kolb, Edward A., Reinhardt, Dirk, Abrahamsson, Jonas, Adachi, Souichi, Aplenc, Richard, De Bont, Eveline S.J.M., De Moerloose, Barbara, Dworzak, Michael, Gibson, Brenda E.S., Hasle, Henrik, Leverger, Guy, Locatelli, Franco, Ragu, Christine, Ribeiro, Raul C., Rizzari, Carmelo, Rubnitz, Jeffrey E., Smith, Owen P., Sung, Lillian, Tomizawa, Daisuke, van den Heuvel-Eibrink, Marry M., Creutzig, Ursula, Kaspers, Gertjan J.L.
Published in Journal of clinical oncology (20.09.2015)
Published in Journal of clinical oncology (20.09.2015)
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Journal Article
Measurable Residual Disease and Fusion Partner Independently Predict Survival and Relapse Risk in Childhood KMT2A-Rearranged Acute Myeloid Leukemia: A Study by the International Berlin-Frankfurt-Münster Study Group
van Weelderen, Romy E., Klein, Kim, Harrison, Christine J., Jiang, Yilin, Abrahamsson, Jonas, Arad-Cohen, Nira, Bart-Delabesse, Emmanuelle, Buldini, Barbara, De Moerloose, Barbara, Dworzak, Michael N., Elitzur, Sarah, Fernández Navarro, José M., Gerbing, Robert B., Goemans, Bianca F., de Groot-Kruseman, Hester A., Guest, Erin, Ha, Shau-Yin, Hasle, Henrik, Kelaidi, Charikleia, Lapillonne, Hélène, Leverger, Guy, Locatelli, Franco, Masetti, Riccardo, Miyamura, Takako, Norén-Nyström, Ulrika, Polychronopoulou, Sophia, Rasche, Mareike, Rubnitz, Jeffrey E., Stary, Jan, Tierens, Anne, Tomizawa, Daisuke, Zwaan, C. Michel, Kaspers, Gertjan J.L.
Published in Journal of clinical oncology (01.06.2023)
Published in Journal of clinical oncology (01.06.2023)
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A Novel l -Asparaginase with low l -Glutaminase Coactivity Is Highly Efficacious against Both T- and B-cell Acute Lymphoblastic Leukemias In Vivo
Nguyen, Hien Anh, Su, Ying, Zhang, Jenny Y., Antanasijevic, Aleksandar, Caffrey, Michael, Schalk, Amanda M., Liu, Li, Rondelli, Damiano, Oh, Annie, Mahmud, Dolores L., Bosland, Maarten C., Kajdacsy-Balla, Andre, Peirs, Sofie, Lammens, Tim, Mondelaers, Veerle, De Moerloose, Barbara, Goossens, Steven, Schlicht, Michael J., Kabirov, Kasim K., Lyubimov, Alexander V., Merrill, Bradley J., Saunthararajah, Yogen, Van Vlierberghe, Pieter, Lavie, Arnon
Published in Cancer research (Chicago, Ill.) (15.03.2018)
Published in Cancer research (Chicago, Ill.) (15.03.2018)
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Journal Article
RAS-pathway mutation patterns define epigenetic subclasses in juvenile myelomonocytic leukemia
Lipka, Daniel B., Witte, Tania, Toth, Reka, Yang, Jing, Wiesenfarth, Manuel, Nöllke, Peter, Fischer, Alexandra, Brocks, David, Gu, Zuguang, Park, Jeongbin, Strahm, Brigitte, Wlodarski, Marcin, Yoshimi, Ayami, Claus, Rainer, Lübbert, Michael, Busch, Hauke, Boerries, Melanie, Hartmann, Mark, Schönung, Maximilian, Kilik, Umut, Langstein, Jens, Wierzbinska, Justyna A., Pabst, Caroline, Garg, Swati, Catalá, Albert, De Moerloose, Barbara, Dworzak, Michael, Hasle, Henrik, Locatelli, Franco, Masetti, Riccardo, Schmugge, Markus, Smith, Owen, Stary, Jan, Ussowicz, Marek, van den Heuvel-Eibrink, Marry M., Assenov, Yassen, Schlesner, Matthias, Niemeyer, Charlotte, Flotho, Christian, Plass, Christoph
Published in Nature communications (19.12.2017)
Published in Nature communications (19.12.2017)
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Patient-reported quality of life after tisagenlecleucel infusion in children and young adults with relapsed or refractory B-cell acute lymphoblastic leukaemia: a global, single-arm, phase 2 trial
Laetsch, Theodore W, Myers, Gary Douglas, Baruchel, André, Dietz, Andrew C, Pulsipher, Michael A, Bittencourt, Henrique, Buechner, Jochen, De Moerloose, Barbara, Davis, Kara L, Nemecek, Eneida, Driscoll, Timothy, Mechinaud, Francoise, Boissel, Nicolas, Rives, Susana, Bader, Peter, Peters, Christina, Sabnis, Himalee S, Grupp, Stephan A, Yanik, Gregory A, Hiramatsu, Hidefumi, Stefanski, Heather E, Rasouliyan, Lawrence, Yi, Lan, Shah, Sweta, Zhang, Jie, Harris, Andrew C
Published in The lancet oncology (01.12.2019)
Published in The lancet oncology (01.12.2019)
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Journal Article
Hematopoietic stem cell transplantation in children and adolescents with GATA2-related myelodysplastic syndrome
Bortnick, Rachel, Wlodarski, Marcin, de Haas, Valerie, De Moerloose, Barbara, Dworzak, Michael, Hasle, Henrik, Masetti, Riccardo, Starý, Jan, Turkiewicz, Dominik, Ussowicz, Marek, Kozyra, Emilia, Albert, Michael, Bader, Peter, Bordon, Victoria, Cario, Gunnar, Beier, Rita, Schulte, Johannes, Bresters, Dorine, Müller, Ingo, Pichler, Herbert, Sedlacek, Petr, Sauer, Martin G., Zecca, Marco, Göhring, Gudrun, Yoshimi, Ayami, Noellke, Peter, Erlacher, Miriam, Locatelli, Franco, Niemeyer, Charlotte M., Strahm, Brigitte
Published in Bone marrow transplantation (Basingstoke) (01.11.2021)
Published in Bone marrow transplantation (Basingstoke) (01.11.2021)
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Synonymous GATA2 mutations result in selective loss of mutated RNA and are common in patients with GATA2 deficiency
Kozyra, Emilia J., Pastor, Victor B., Lefkopoulos, Stylianos, Sahoo, Sushree S., Busch, Hauke, Voss, Rebecca K., Erlacher, Miriam, Lebrecht, Dirk, Szvetnik, Enikoe A., Hirabayashi, Shinsuke, Pasaulienė, Ramunė, Pedace, Lucia, Tartaglia, Marco, Klemann, Christian, Metzger, Patrick, Boerries, Melanie, Catala, Albert, Hasle, Henrik, de Haas, Valerie, Kállay, Krisztián, Masetti, Riccardo, De Moerloose, Barbara, Dworzak, Michael, Schmugge, Markus, Smith, Owen, Starý, Jan, Mejstrikova, Ester, Ussowicz, Marek, Morris, Emma, Singh, Preeti, Collin, Matthew, Derecka, Marta, Göhring, Gudrun, Flotho, Christian, Strahm, Brigitte, Locatelli, Franco, Niemeyer, Charlotte M., Trompouki, Eirini, Wlodarski, Marcin W.
Published in Leukemia (01.10.2020)
Published in Leukemia (01.10.2020)
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Brachytherapy for Pediatric Patients at Gustave Roussy Cancer Campus: A Model of International Cooperation for Highly Specialized Treatments
Chargari, Cyrus, Haie-Meder, Christine, Espenel, Sophie, Garcia, Max-Adrien, Ben-Arush, Myriam, Bolle, Stéphanie, Borjesson, Anna, Cesen, Maja, Lago, Rita Costa, Defachelles, Anne-Sophie, De Moerloose, Barbara, Devalck, Christine, Edslev, Pernille, Farinha, Nuno Jorge, Francotte, Nadine, Glosli, Heidi, Gouy, Sebastien, Burrieza, Gabriela Guillen, Helfre, Sylvie, Irtan, Sabine, Kattamis, Antonis, Lacerda, Ana, Levy, Antonin, Hjalgrim, Lisa Lyngsie, Mansuy, Ludovic, Mascard, Eric, Moalla, Salma, Orbach, Daniel, Owens, Cormac, Philippe-Chomette, Pascale, Pizer, Barry, Pluchart, Claire, Renard, Marleen, Rognlien, Anne Gro Wesenberg, Rome, Angélique, Sarnacki, Sabine, Safwat, Akmal, Schiavetti, Amalia, Serre, Jill, Verite, Cécile, Weid, Nicolas Von Der, Wysocki, Mariusz, Valteay-Couanet, Dominique, Deutsch, Eric, Minard-Colin, Véronique, Martelli, Hélène, Guérin, Florent
Published in International Journal of Radiation OncologyBiologyPhysics (01.07.2022)
Published in International Journal of Radiation OncologyBiologyPhysics (01.07.2022)
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In vivo stabilization of a less toxic asparaginase variant leads to a durable antitumor response in acute leukemia
Van Trimpont, Maaike, Schalk, Amanda M., De Visser, Yanti, Nguyen, Hien Anh, Reunes, Lindy, Vandemeulebroecke, Katrien, Peeters, Evelien, Su, Ying, Lee, Hyun, Lorenzi, Philip L., Chan, Wai-Kin, Mondelaers, Veerle, De Moerloose, Barbara, Lammens, Tim, Goossens, Steven, Van Vlierberghe, Pieter, Lavie, Arnon
Published in Haematologica (Roma) (01.02.2023)
Published in Haematologica (Roma) (01.02.2023)
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Characteristics and outcome of primary resistant disease in paediatric acute myeloid leukaemia
Karlsson, Lene, Cheuk, Daniel, De Moerloose, Barbara, Hasle, Henrik, Jahnukainen, Kirsi, Juul‐Dam, Kristian Løvvik, Kaspers, Gertjan, Kovalova, Zanna, Lausen, Birgitte, Nyström, Ulrika Norén, Palle, Josefine, Pronk, Cornelis Jan, Saks, Kadri, Tierens, Anne, Zeller, Bernward, Abrahamsson, Jonas
Published in British journal of haematology (01.05.2023)
Published in British journal of haematology (01.05.2023)
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Characterization of Pediatric Acute Myeloid Leukemia With t(7;12)(q36;p13)
Östlund, Anders, Waraky, Ahmed, Staffas, Anna, Sjögren, Helene, De Moerloose, Barbara, Arad‐Cohen, Nira, Cheuk, Daniel, Navarro, Jose Maria Fernandez, Jahnukainen, Kirsi, Kaspers, Gertjan J. L., Kovalova, Zhanna, Pasauliene, Ramune, Saks, Kadri, Zeller, Bernward, Norén‐Nyström, Ulrika, Hasle, Henrik, Fogelstrand, Linda, Abrahamsson, Jonas, Palmqvist, Lars
Published in Genes chromosomes & cancer (01.11.2024)
Published in Genes chromosomes & cancer (01.11.2024)
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Targeting hyperactive platelet-derived growth factor receptor-β signaling in T-cell acute lymphoblastic leukemia and lymphoma
De Coninck, Stien, De Smedt, Renate, Lintermans, Beatrice, Reunes, Lindy, Kosasih, Hansen J., Reekmans, Alexandra, Brown, Lauren M., Van Roy, Nadine, Palhais, Bruno, Roels, Juliette, Van der Linden, Malaika, Van Dorpe, Jo, Ntziachristos, Panagiotis, Van Delft, Frederik W., Mansour, Marc R., Pieters, Tim, Lammens, Tim, De Moerloose, Barbara, De Bock, Charles E., Goossens, Steven, Van Vlierberghe, Pieter
Published in Haematologica (Roma) (01.05.2024)
Published in Haematologica (Roma) (01.05.2024)
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Deciphering molecular heterogeneity in pediatric AML using a cancer vs. normal transcriptomic approach
Depreter, Barbara, De Moerloose, Barbara, Vandepoele, Karl, Uyttebroeck, Anne, Van Damme, An, Terras, Eva, Denys, Barbara, Dedeken, Laurence, Dresse, Marie-Françoise, Van der Werff Ten Bosch, Jutte, Hofmans, Mattias, Philippé, Jan, Lammens, Tim
Published in Pediatric research (01.05.2021)
Published in Pediatric research (01.05.2021)
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